First-in-the-world gene therapy delivers missing gene directly to infant’s brain, marking historic milestone in precision medicine
On Jun. 8, 2026, an eight-month-old infant with a severe genetic epilepsy has become the first patient in…
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New CDKL genes linked to neurodevelopmental disorders
On Apr. 3, 2025, a team led by researchers at Baylor College of Medicine and the Jan and…
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Biotechnology | Clinical Research | Diagnostics | Disease | Neurology | Non-Profit Research | Therapeutics
CIRM Approves New and Updated Funding Programs, Awards $26.5 Million for Clinical Research and Development
On Mar. 27, 2025, the California Institute for Regenerative Medicine (CIRM), one of the world’s largest institutions dedicated…
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Exome sequencing of more than 54,000 individuals with epilepsy revealed genetic links
On Oct. 3, 2024, scientists announced the largest whole-exome sequencing study of epilepsy to date, with more than…
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Breakthrough Gene Therapy Offers Hope for Severe Developmental Epilepsy in Children
On Jun. 27, 2023, researchers from Tel Aviv University announced they have developed an innovative gene therapy that…
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Study suggested no association between antiseizure drugs used during pregnancy and neurodevelopmental problems in children at age 2
On Jun. 7, 2021, the National Institutes of Health announced new findings published in JAMA Neurology that suggested…
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FDA approved new indication for drug containing an active Cannabis ingredient to treat seizures in rare genetic disease
On Jul. 31, 2020, the U.S. Food and Drug Administration (FDA) announced it had approved Epidiolex (cannabidiol) [CBD]…
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The FDA approved new therapy for Dravet Syndrome
On Jun. 25, 2020, the U.S. Food and Drug Administration (FDA) approved Fintepla (fenfluramine), a Schedule IV controlled…
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Neurology | NIH | Therapeutics
Scientists monitored brains replaying memories in real time
On Mar. 5, 2020, in a study of epilepsy patients, researchers at the National Institutes of Health (NIH)…
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FDA approved first drug comprised of an active ingredient derived from marijuana to treat epilepsy
On Jun. 25, 2018, the U.S. Food and Drug Administration (FDA) approved Epidiolex (cannabidiol) [CBD] oral solution for…
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Doernbecher Children’s Hospital opened first pediatric intraoperative MRI facility on the West Coast
On Feb. 3, 2016, OHSU Doernbecher Children’s Hospital unveiled a 3-Tesla intraoperative magnetic resonance imaging machine that provides…
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Biotechnology | Diagnostics | Disease | NIH | Therapeutics
The McDonnell Genome Institute received a $60 million from the NIH to study the genetics of common diseases
On Jan. 19, 2016, the McDonnell Genome Institute at Washington University School of Medicine in St. Louis announced…
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The Allen Institute for Brain Science Completed the Brain Atlas
On Sept. 26, 2006, the Allen Institute for Brain Science announced the completion of the groundbreaking Allen Brain…
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Roger W. Sperry was awarded Nobel Prize in Medicine
In 1981, Roger W. Sperry of the California Institute of Technology was awarded the Nobel Prize in Physiology…
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The term ‘developmental disability’ was introduced
In 1970, the term ‘developmental disability’ is introduced in the Developmental Disabilities Services and Facilities construction amendments to…
