The FDA approved new therapy for rare disease affecting optic nerve, spinal cord
On Jun. 11, 2020, the U.S. Food and Drug Administration approved Viela Bio’s Uplizna (inebilizumab-cdon) injection for intravenous…
On Jun. 11, 2020, the U.S. Food and Drug Administration approved Viela Bio’s Uplizna (inebilizumab-cdon) injection for intravenous…
On May 7, 2020, the National Institutes of Health (NIH) announced a new online survey launched by the…
On Apr. 10, 2020, the U.S. Food and Drug Administration (FDA) approved selumetinib (KOSELUGO, AstraZeneca) for pediatric patients, 2…
On Mar. 31, 2020, researchers at the National Institutes of Health announced they had discovered a second gene…
On Aug. 15, 2019, the Cancer Prevention and Research Institute of Texas (CPRIT) announced that it was awarded…
On Feb. 25, 2019, the Tyrosinemia Society (TS, Inc.) was founded by Dr. Elizabeth Barnby, a researcher and…
On Aug. 15, 2017, the National Institutes of Health’s (NIH) Gabriella Miller Kids First Pediatric Research Program awarded…
On Jun. 17, 2014, Grifols celebrated the grand opening of its new state-of-the-art North Fractionation Facility (NFF) in…
On May 16, 2012, the U.S. Senate unanimously passed a resolution (S. Res. 286) recognizing May 16, 2012,…
On Mar. 2, 2008, Adult stem cells may provide an explanation for the cause of a Hutchinson-Gilford Progeria…
On Feb. 28, 2008, Rare Disease Day (also known as an “orphan” disease) is a globally coordinated movement…
On Sept. 24, 2007, Duke University announced it will receive $35 million from billionaire real estate developer David…
In 2001, the Stephenson Cancer Center was established. Located on the University of Oklahoma (OU) Health Sciences Center…
On Oct. 25, 1996, the first gene therapy trial for patients with Hunter syndrome was begun at the…
In 1987, the U.S. Food and Drug Administration (FDA) announced revised regulations regarding Expanded Access (EA) to investigational…
On Jan. 3, 1983, the Orphan Drug Act was passed by the U.S. Congress with the leadership of…
On Jun. 5, 1981, Dr. Michael Gottlieb and colleagues of University of California at Los Angeles reported a…
In 1976, the U.S. Centers for Disease Control and Prevention (CDC) was involved in a national immunization program…
In 1963, Australian pathologist R.D.K. Reye first described this syndrome. National surveillance led to strict warnings regarding aspirin…
On Jan. 12, 1961, the National Cancer Institute (NCI) established the Laboratory of Viral Oncology, a new intramural…
In 1959, Johnson ᅠ&ᅠ Johnson acquired McNeil Laboratories giving the Company a significant presence in the growing field…
In 1940, the U.S. government established a national blood collection program. That same year the National Research Council…